Rare diseases affect one in 10 people.

CMT4J is a rare, progressive, neurological disease similar to ALS.

CureCMT4J is a non-profit created by parents of Talia, a teenage girl with severe, early-onset CMT4J. CureCMT4J is the only entity working toward a treatment or cure for this deadly disease. YOU can help us to get there. 

Chase the Butterfly is BACK!

Join us on Sunday, May 4th at 10 a.m. for our annual, can’t-miss 5K road race. This year we’ve teamed up with the Ipswich Family YMCA, and the run will take place on the beautiful New England Biolabs campus. Let’s bring the community together for the sixth annual run/walk/roll!

$1,517,315
OF OUR $2,200,000 GOAL

CURECMT4J IS DRIVING RESEARCH TOWARD TREATMENTS

Our researchers working together from The Jackson Laboratory, UT Southwestern, and University of Michigan have shown great success in using gene therapy to treat CMT4J mouse models! We’re working hard on getting it into a clinical trial! 

Gene Therapy

Drug Repurposing

To learn more about our research visit our Research Pathway page

Help us spread the word!

Watch our latest videos below, and then share them by clicking the arrow icon in the upper-right corner. Thanks!